Tag: SOD1 September 21, 2022 Investigational drug for genetic form of ALS improves disease’s molecular signsExtended use of tofersen may help stabilize muscle strength, control.News Release July 8, 2020 Experimental drug shows early promise against inherited form of ALS, trial indicatesPhase 1/phase 2 trial shows evidence for safety, biological activity of tofersen; phase 3 trial underway.News Release January 6, 2020 Miller receives international innovation prizeRecognized for developing experimental treatment for ALS.National Leaders July 16, 2018 New ALS therapy in clinical trialsDrug extends survival, reverses some neuromuscular damage in animals.News Release Posts navigation