Tag: lysosomal storage diseases March 8, 2022 Kornfeld receives Roscoe O. Brady AwardHematologist honored for lysosomal disease research.National Leaders September 16, 2019 Cause of rare, fatal disorder in young children pinpointedProof-of-concept drug therapy benefits mouse model of Krabbe disease.News Release July 30, 2019 Half-century of research illuminates how cells work in health, diseaseKornfeld reflects on knowledge gained from longest running NCI grant.News Release Posts navigation