Tag: antisense oligonucleotides (ASO) April 25, 2023 Drug for rare form of ALS, based in part on WashU research, approved by FDAWashington University neurologist led international trials of the drug, tofersen.News Release, Video July 8, 2020 Experimental drug shows early promise against inherited form of ALS, trial indicatesPhase 1/phase 2 trial shows evidence for safety, biological activity of tofersen; phase 3 trial underway.News Release August 15, 2019 Antisense drugs for Huntington’s, ALS and prion diseases could meet the dire need for brain treatmentsSource: Scientific American July 16, 2018 New ALS therapy in clinical trialsDrug extends survival, reverses some neuromuscular damage in animals.News Release Posts navigation