Tag: tofersen April 25, 2023 Drug for rare form of ALS, based in part on WashU research, approved by FDAWashington University neurologist led international trials of the drug, tofersen.News Release, Video September 21, 2022 Investigational drug for genetic form of ALS improves disease’s molecular signsExtended use of tofersen may help stabilize muscle strength, control.News Release Posts navigation